Baseline IPSS-M, Not Therapy Before HSCT, Predicts MDS Outcomes Rare Disease Advisor 23:56 Mon, 03 Aug
HSCT for Leukemia in Patient With FA Improves Blood Frataxin but Not Neurologic Progression Rare Disease Advisor 21:23 Mon, 03 Aug
AstraZeneca's Ultomiris Hsct-Tma Trial Shows Mixed Results; Pediatric Data Show Survival Benefit RTT News 16:09 Mon, 27 Jul
Patients With MDS Receiving HSCT Have Higher In-Hospital Mortality Rare Disease Advisor 22:29 Mon, 20 Jul