FDA Advisory Committee Votes Against Deramiocel for DMD Cardiomyopathy Rare Disease Advisor 17:37 Fri, 31 Jul
FDA AdCom shuns Capricor’s DMD cell therapy amid data dispute Pharmaceutical Technology 15:06 Thu, 30 Jul
Resin peace, Capricor? SAP spat, weak data foil Dmd adcom bid BioWorld 22:38 Wed, 29 Jul Article paywall
Deramiocel cell therapy slows muscle and heart damage in advanced DMD News-Medical.Net 16:53 Wed, 29 Jul
Should FDA Priority Review of Dyne’s DMD Drug Candidate Reshape Risk Expectations for Dyne Therapeutics (DYN) Investors? Simply Wall St 18:09 Tue, 21 Jul
FDA Decision on Exon 51-Skipping DMD Therapy Z-Rostudirsen Expected in January 2027 Rare Disease Advisor 23:30 Mon, 20 Jul
AI-Designed Aptamer May Improve on Strategy of Discontinued DMD Therapy Pamrevlumab Rare Disease Advisor 22:29 Mon, 20 Jul
Researchers Uncover Rare Genetic Cause of DMD Manifestations in 6 Women Rare Disease Advisor 17:44 Mon, 20 Jul
Vamorolone Associated With Fewer Bone-Related Adverse Events Than Deflazacort in DMD Rare Disease Advisor 23:10 Fri, 17 Jul
When to Schedule an Orthodontic Visit for Children Covered in HelloNation, Featuring Expert Orthodontist Dr. Michelle Mathieson, Dmd, Msd PR Newswire (Press Release) 20:52 Fri, 17 Jul
DMD Gene Therapy Meta-Analysis Shows ‘Modest but Clinically Meaningful’ Effect Rare Disease Advisor 18:20 Wed, 15 Jul
Interim TRAILHEAD Results Show SAT-3247 Improves Muscle Health in Adults With DMD Rare Disease Advisor 18:24 Tue, 14 Jul
Tegacorat Receives FDA Orphan Drug, Rare Pediatric Disease Designations for DMD Rare Disease Advisor 21:19 Mon, 13 Jul
Satellos’ oral DMD drug improves arm movement after six months in Phase II Clinical Trials Arena 11:25 Thu, 09 Jul
Counseling Recorded for Only a Quarter of Children With DMD and Mental Health Needs Rare Disease Advisor 21:42 Wed, 08 Jul
Experts Rate ChatGPT 4 out of 5 or Better as an Information Source for DMD Families Rare Disease Advisor 20:51 Wed, 08 Jul
HelloNation Explains Dental Implant Surgery Recovery With Insights From Dental Implants Professional Dr. Steven Dodson, Dmd PR Newswire (Press Release) 21:15 Mon, 06 Jul