Weekend reads: Young girl’s death after gene therapy never made public; FDA retracts lettuce test result; Ada delays editorial publication after controversy Retraction Watch 14:13 Sat, 25 Jul
Sickle cell gene therapy cure comes with access challenges for Louisiana patients KALB 02:12 Sat, 25 Jul
World first gene therapy treats rare form of childhood blindness Epsom and St Helier University Hospitals (Press Release) 10:42 Fri, 24 Jul
Apertura Gene Therapy Named to Consortium Receiving Funding from the Advanced Research Projects Agency for Health (Arpa-H) thrive Program to Develop Gene Therapies for Rare Childhood Diseases PR Newswire (Press Release) 17:05 Thu, 23 Jul
11-year-old girl is first UK patient to have gene therapy to halt sight loss indy100 06:00 Thu, 23 Jul Article paywall
FDA Expands CRISPR Gene Therapy Casgevy to Children as Young as 2 with Sickle Cell Disease Medical Daily 16:06 Tue, 21 Jul
Tailored gene therapy dramatically reduces childhood epilepsy seizures in trial News-Medical.Net 15:01 Tue, 21 Jul
Personalized Gene Therapy Helps Teen with Rare Form of Severe Epilepsy Walk Independently UC San Diego News Center 10:03 Tue, 21 Jul
Dramatic Results Seen With Gene Therapy for Age-Related Macular Degeneration Medpage Today 17:47 Mon, 20 Jul
Regenxbio Prices $100M Public Offering To Advance Gene Therapy Programs; Stock Down RTT News 15:23 Fri, 17 Jul
STAT Plus: Can ultrasound unlock the power of gene therapy? A startup makes big claims STAT 09:34 Fri, 17 Jul
Circio And Avenue Biosciences Launch Gene Therapy Research Collaboration On Protein Secretion American Pharmaceutical Outsourcing (Press Release) 14:13 Thu, 16 Jul
Older Women May Face Higher Risks from Gene Therapy for Eye Diseases Knowridge Science Report 14:03 Thu, 16 Jul
Gene therapy restores key features in fragile X syndrome mouse model Drug Target Review 09:06 Thu, 16 Jul
Ocugen, Inc. Announces Binding Term Sheet with Roots Pharmaceutical to License OCU400Modifier Gene Therapy for Retinitis Pigmentosa in the Middle East and North Africa Riyadh Daily 21:07 Wed, 15 Jul
DMD Gene Therapy Meta-Analysis Shows ‘Modest but Clinically Meaningful’ Effect Rare Disease Advisor 18:20 Wed, 15 Jul
Immuneel, Tata Memorial Centre partner to advance cell and gene therapy research The Hindu Business Line 13:47 Wed, 15 Jul
EpilepsyGTx selects ClearPoint Neuro technology for Phase I/IIa epilepsy gene therapy trial Manufacturing Chemist 12:25 Wed, 15 Jul
EpilepsyGTx partners with ClearPoint Neuro to support targeted delivery of lead gene therapy in epilepsy News-Medical.Net 11:38 Tue, 14 Jul
Gene therapy shows durable correction of methylmalonic acidemia in preclinical study Drug Target Review 13:08 Fri, 10 Jul
Apertura and NIH institutes to test gene therapy for NPC1 Pharmaceutical Technology 10:15 Fri, 10 Jul
Patients win 1st damages ruling against Kolon over Invossa gene therapy Korea Biomedical Review 09:01 Fri, 10 Jul
Apertura Gene Therapy Announces Cooperative Research and Development Agreement with Institutes of the NIH to Test Investigational Gene Therapy for Niemann-Pick Disease Type C1 PR Newswire (Press Release) 13:03 Thu, 09 Jul
GC Cell's Immunecell-LC Inj. is added to WHO's ATC classification for antineoplastic cell and gene therapy Korea Biomedical Review 05:39 Thu, 09 Jul
FDA Expands Use of First Sickle Cell Disease Gene Therapy for Children as Young as 2 Years HealthDay 21:48 Wed, 08 Jul
How a CRISPR Gene Therapy Could Change Life for Young Children With Sickle Cell Disease Discover Magazine 21:32 Wed, 08 Jul
Weill Cornell Medicine receives federal grant to study new gene therapy for Alzheimer's disease News-Medical.Net 19:38 Wed, 08 Jul
New gene therapy strategy uses the brain's own glymphatic transport system for drug delivery News-Medical.Net 13:42 Wed, 08 Jul
Genespire and Sr-Tiget Show Durable Preclinical Efficacy of Liver-Directed Gene Therapy for Methylmalonic Acidemia PR Newswire (Press Release) 08:03 Wed, 08 Jul
Bio-Rad launches Vericheck ddPCR Kits compatible with QX700 platform for biopharma quality control and cell and gene therapy workflows News-Medical.Net 05:44 Wed, 08 Jul